Thank you to our speakers, sponsors, and delegates
who joined us in Boston for the summit!
Welcome to the 8th Gene Therapy Development Summit
Your Flagship Gene Therapy Forum Providing Cutting-Edge Updates across Translation, Clinical, Manufacturing & Commercialization
With 14 new gene therapy approvals in the last 18 months, billion-dollar collaborations, and the development of treatments for more common conditions, the gene therapy field is rapidly gaining momentum and broadening its scope beyond rare diseases. The new and improved 8th Gene Therapy Development Summit, formerly known as the Gene Therapy for Rare Disorders Summit, united senior leaders from the likes of Pfizer, REGENXBIO, Vertex, Vivet Therapeutics, Carbon Biosciences, Beam Therapeutics, and the FDA to tackle the field’s biggest challenges of achieving genuine scalability and accessibility to meet growing patient demand.
This unique opportunity provided attendees full visibility of cutting-edge developments from translation through to commercialization, gaining full competitor insight to benchmark novel approaches and inform and fast-track their gene therapy through the clinic, expanding their patient reach.
Key Themes You Missed Out On:
Scaling Gene Therapy
Expanding from Rare to Common Diseases with Efficiency & Market Readiness
Next-Gen Delivery
Advancing Beyond AAV for Precision Gene Therapy Targeting
From Lab to Market
Unlocking Funding, Access, and Commercial Success for Gene Therapies
Innovating for Safety & Precision
The Future of AI, Gene Editing, and Targeted Therapies
Manufacturing Excellence
Scaling Up Gene Therapy with Cost-Effective & High-Quality Production
We united industry professionals to drive gene therapy innovation across translational, clinical, and manufacturing tracks. This event was designed to help attendees navigate the entire gene therapy pipeline.
By refining gene delivery platforms, optimizing manufacturing processes, and navigating regulatory pathways, we can revolutionize the future of gene therapies—bringing them to broader patient populations and significantly enhancing clinical outcomes.
2025 World-Class Speaker Faculty Includes:





Sebastian Aguirre Kozlouski
Co-Founder, Vice President, Head of Platform Development
Carbon Biosciences
Previously Attending Companies Include:

Our 2025 Partners:












